SPINRAZA: MEDICINE FOR SPINAL MUSCULAR ATROPHY - AND MEDICATION

Spinraza: medicine for spinal muscular atrophy



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46 Almeida Prado
46 Almeida Prado
Spinraza is a drug that takes the SMN-2 gene to produce a protein that is normally produced by the SMN-1 gene, replacing it. Thus, this medication is used to treat cases of spinal muscular atrophy, which develops due to lack or defect of the SMN-1 gene in the body. Although this drug has already been approved in the United States by the FDA and is being used as a treatment in the hospital, it still needs Anvisa's approval in Brazil